About this webinar
Neurogenetic disorders that impact how the brain functions affect up to three percent of children, but available evaluation tools arenāt sensitive enough to detect change in their developmental skills. This poses a challenge for clinical trial sponsors who are trying to assess potential treatments. In addition, detailed natural history studies havenāt done enough to characterize the effects of age and the stage of disease of neurogenetic disorders.Ā
Recent research has been calling for new and improved tools to test treatments of all pediatric neurogenetic diseases ā something researchers and trial sponsors are eager to see. Join experts for a one-hour webinar that will help you better understand the challenges to treatment in these trial settings. Ā
Youāll learn:
Why available evaluation tools may not always be effective in clinical trials
The advantages of precise tools and metrics in developing clinical trial protocols
Why Growth Scale Values (GSVs) are a better metric for measuring developmental change during trialsĀ